Collection of safety and efficacy data once a drug has received conditional marketing approval
Find out about DMD care in 24 languages - including Slovak & Korean!
The importance of genetic diagnosis for Duchenne muscular dystrophy
TREAT-NMD Advisory Committee for Therapeutics - application & review process, past reviews, committee etc
Service overview: trial sites and patients, advisory support, study support, training
By supporting the work of the TREAT-NMD Alliance you can help us advance research
A unique network of biobanks storing quality DNA, cell & tissue samples on rare diseases and NMDs
Download the TREAT-NMD brochure here