Post marketing surveillance

Collection of safety and efficacy data once a drug has received conditional marketing approval


Latest publications!
Care guidelines for DMD & SMA - significant updates published


Service overview: trial sites and patients, advisory support, study support, training



TREAT-NMD Advisory Committee for Therapeutics - application & review process, past reviews, committee etc



A unique network of biobanks storing quality DNA, cell & tissue samples on rare diseases and NMDs

Imperatives of DMD

Find out about DMD care in 24 languages - including Slovak & Korean!

Donate to TREAT-NMD

By supporting the work of the TREAT-NMD Alliance you can help us advance research

Our Brochure

Our Brochure

Our brochure is available to download here!!