Tuesday, 26th March 2019

DMD Guide for Families

New 2018 DMD Guide for Families now available in US & UK.

Post marketing surveillance

Collection of safety and efficacy data once a drug has received conditional marketing approval


Latest publications!
Care guidelines for DMD & SMA - significant updates published



Download our industry brochure
Trial sites and patients, advisory support, study support, training



TREAT-NMD Advisory Committee for Therapeutics - application & review process, past reviews, committee etc


A unique network of biobanks storing quality DNA, cell & tissue samples on rare diseases and NMDs

Donate to TREAT-NMD

By supporting the work of the TREAT-NMD Alliance you can help us advance research

Our Brochure

Our Brochure

Our brochure is available to download here!!