Post marketing surveillance

Collection of safety and efficacy data once a drug has received conditional marketing approval

Publications

Latest publications!
Care guidelines for DMD & SMA - significant updates published

Industry

Service overview: trial sites and patients, advisory support, study support, training

 

TACT

TREAT-NMD Advisory Committee for Therapeutics - application & review process, past reviews, committee etc

 

BioBanks

A unique network of biobanks storing quality DNA, cell & tissue samples on rare diseases and NMDs

Imperatives of DMD

Latest!!
Find out about DMD care in 24 languages - including Slovak & Korean!

Donate to TREAT-NMD

By supporting the work of the TREAT-NMD Alliance you can help us advance research

 
Our Brochure

Our Brochure

Our brochure is available to download here!!