Post marketing surveillance

Collection of safety and efficacy data once a drug has received conditional marketing approval

Imperatives of DMD

Find out about DMD care in 24 languages - including Slovak & Korean!



Latest publication!
The importance of genetic diagnosis for Duchenne muscular dystrophy


TREAT-NMD Advisory Committee for Therapeutics - application & review process, past reviews, committee etc



Service overview: trial sites and patients, advisory support, study support, training

Donate to TREAT-NMD

By supporting the work of the TREAT-NMD Alliance you can help us advance research


A unique network of biobanks storing quality DNA, cell & tissue samples on rare diseases and NMDs

2016 Brochure

2016 Brochure

Our NEW 2016 brochure is available to download here!!