Duchenne muscular dystrophy

Duchenne muscular dystrophy

This section brings together information about Duchenne muscular dystrophy from across the website. Much of the information here is especially relevant for individuals and families affected by DMD, but family doctors and researchers should also find something of interest.

Browse through this section for specific information about DMD, and also take a look at the other areas of our website for more general information about TREAT-NMD and the resources we offer.

Family care guide now available on tablets and smartphones!

UK Clinical Trial Capacity Workshop

About DMD

An overview of Duchenne muscular dystrophy - how it is caused, how it is inherited, and what its symptoms are

Patient registries

Register in your national DMD patient registry and become part of the international TREAT-NMD registry for people with DMD around the world

 

Academic article on care standards

An international consensus document setting out best practice in care for DMD was published in the Lancet Neurology journal in January and February 2010

Family guide on care standards

A comprehensive family guide based on the full academic care standards article has been produced to give families the power to discuss their care with care providers

 

Overview of research strategies

Information for patients and parents about the different therapeutic approaches for DMD currently under investigation and the stage each has reached

Clinical research and trials

Find out about current clinical research and trials and see a list of ongoing DMD trials Latest - download DMD UK clinical trial capacity workshop

 

Research resources

Information on resources available to Duchenne researchers, including standards for preclinical efficacy studies, molecular testing best-practice guidelines, and the Registry of Outcome Measures (ROM)

Patient organizations

See a list of patient organizations and advocacy groups providing support for DMD patients and families across the world

 
 
27 Nov 2015