PPMD Conference 2012

27 Jun 2012 - 1 Jul 2012

Fort Lauderdale, Florida, USA

28 June - 1 July 2012, Fort Lauderdale, USA

This year's annual Parent Project Muscular Dystrophy conference was attended by extended families of Duchenne patients, as well as industry representatives, clinicians, scientists and this year a large delegation of physiotherapists and physiotherapy students from Florida.

The program was packed with presentations on new therapeutic approaches, some of which are currently tested in clinical trials, such as exon skipping (tested in over 200 Duchenne patients), utrophin upregulation (tested in healthy volunteers), PDE5 inhibitors (to improve muscle bloodflow, encouraging results obtained in Becker muscular dystrophy patients) and numerous compounds to improve muscle quality and/or inhibit fibrosis.

In addition there was a session on good quality care and there were interactive workshops on everyday aspects of the disease for parents, siblings and grandparents of patients, and on physiotherapy and stretching, and fundraising.

For the first time this year there were user panels on clinicial trial participation, where parents, clinicians, industry employees and patients openly discussed the different aspects and perspectives of participating in a clinical trial.

Highlights of the meeting were the keynote lecture by Rick Guidotti, a fashion photographer, who currently takes pictures of children with genetic diseases or malformations to show their beauty and to change the way society sees them and a speech from Luca Buccella, an adult Duchenne patient, during the gala dinner, which can be viewed here.

Harbor Beach Marriott
Ft. Lauderdale

Placeholder for GoogleMap. Use the preview button to see the real map.