Companies working with TREAT-NMD

In one form or another, TREAT‐NMD is assisting many companies currently planning or running neuromuscular trials. It is also involved in investigator-led research, and many TREAT-NMD partners are also experienced trial sites taking part in neuromuscular trials.

The list below gives brief details on each company, contact details and links to their respective websites.

Acceleron Pharma Acceleron Pharma

United States of America

Acceleron is a privately held biopharmaceutical company committed to discover, develop, manufacture and commercialize novel biotherapeutics that modulate the growth of red blood cells, bone, muscle, fat and the vasculature to treat musculoskeletal, metabolic and cancer-related diseases.

Drug For disease Status
ACE‐031 DMD Ongoing - see details on clinicaltrials.gov
     

More Info
Website www.acceleronpharma.com

 

BioMarin Pharmaceutical Inc BioMarin Pharmaceutical Inc

United States of America

Founded in 1997 BioMarin has developed and commercialized four products in this time. With over 700 employees and a head office in California, clinical research is conducted on an international scale with the main area of focus being rare 'orphan' genetic diseases.

More Info
Website www.bmrn.com

 

Csimma LLC

United States of America

 

Généthon Généthon

France

First a pioneer of human genome research, Genethon now explores the new therapeutic hypotheses stemming from the extraordinary progresses of contemporary biology.

More Info
Website www.genethon.fr

 

Genzyme Corporation Genzyme Corporation

United States of America

One of the world's leading biotechnology companies, Genzyme is dedicated to making a major positive impact on the lives of people with serious diseases. Since 1981, the company has grown from a small start-up to a diversified enterprise with approximately 10,000 employees in locations spanning the globe and 2009 revenues of $4.5 billion.

More Info
Website www.genzyme.com

 

Glaxo Smithkline Glaxo Smithkline

United Kingdom

GlaxoSmithKline produce medicines that treat major disease areas such as asthma, virus control, infections, mental health, diabetes and digestive conditions. In addition, they are a leader in the important area of vaccines and are developing new treatments for cancer.

More Info
Website www.gsk.com

 

Novamen Novamen

France

NOVAMEN, member of ACIES Consulting Group, specializes in collaborative research management, accompanies private and public stakeholders in European research in the strategic and operational management of their collaborative research projects, with a particular focus on European Union Framework Projects.

More Info
Website www.novamen.eu

 

Pfizer Pfizer

United States of America

Since Pfizer was founded by cousins Charles Pfizer and Charles Erhart in 1849, the pharmaceutical company has remained dedicated to discovering and developing new, and better, ways to prevent and treat disease and improve health and well being for people around the world.

More Info
Website www.pfizer.com

 

Prosensa Prosensa

Netherlands

Prosensa is a biopharmaceutical company focused on the discovery, development and commercialization of RNA modulating therapeutics. The company targets genetic disorders with a large unmet medical need, with a primary focus on neuromuscular disorders.

More Info
Website www.prosensa.eu

 

PTC Therapeutics PTC Therapeutics

United States of America

PTC Therapeutics, Inc. is a biopharmaceutical company focused on the discovery, development and commercialization of orally administered, proprietary small-molecule drugs that target post-transcriptional control processes.

More Info
Website www.ptcbio.com

 

Roche Roche

Switzerland

As a research-focused healthcare company, Roche discovers, develops and provides innovative diagnostic and therapeutic products and services that deliver significant benefits to patients and healthcare professionals – from early detection and prevention of diseases to diagnosis, treatment, and treatment monitoring.

More Info
Website www.roche.com

 

Santhera Pharmaceuticals Santhera Pharmaceuticals

Switzerland

Santhera Pharmaceuticals (SIX: SANN) is a Swiss specialty pharmaceutical company focusing on the development and marketing of innovative pharmaceutical products for the treatment of orphan neuromuscular diseases. Santhera currently has three compounds in seven clinical-stage development programs.

More Info
Website www.santhera.com

 

Sarepta Sarepta

United States of America

Sarpeta's vision is to transform how the world approaches the treatment of serious and life-threatening diseases by unlocking the potential of RNA technologies.

Recognizing the complexity of this goal, they focus on rare and infectious diseases with tremendous unmet needs—areas in which new therapies have the potential to make dramatic improvements in the lives of patients.

More Info
Website www.sarepta.com

 

Shire Shire

Ireland

Shire plc is a rapidly growing global specialty biopharmaceutical company.

Shire has a global sales and marketing infrastructure with a broad portfolio of products and its own direct marketing capability in the US, Canada, UK, Republic of Ireland, France, Germany, Belgium, Italy and Spain.

More Info
Website www.shire.com

 

Summit PLC Summit PLC

United Kingdom

Summit is an Oxford, UK based drug discovery company with an innovative technology platform called Seglins for the discovery of new medicines, a portfolio of partner funded drug programmes and a commercial strategy of signing multiple early-stage deals.

More Info
Website www.summitplc.com

 

Trophos Trophos

France

Founded in 1999 Trophos has 25 employees and is based in Marseille, France. Trophos is a clinical stage pharmaceutical company developing innovative therapeutics for indications with under-served needs in neurology and cardiology.

More Info
Website www.trophos.com

 
 
10 Feb 2011