Resources overview

Care overview

• DMD care
• SMA care
• CMD care
• Genetic testing

Global patient registries

• Registries overview
• Registries: patient information
• National DMD registries
• National SMA registries
• CMD International Registry
• National patient registries for myotonic dystrophy
• International FKRP registry
• Rare NMD registries
• Registries toolkit
• Patient registries: use by industry
• Patient registries - FAQ

Neuromuscular care and trial centres

• Care and trial site registry

TACT

• Introduction
• Committee members
• Application process
• Guidance
• Reviews

Outcome measures

• About outcome measures
• Outcome measures research
• Registry of outcome measures
• NMR as an outcome measure
• Functional evaluation tools

Biobanks

• EuroBioBank

Social and ethical framework

• Social and ethical research
• Project Ethics Council
• Supporting gender equality
• Guide to patient involvement in research
• Stem cells
• Ethical tutorial children in trials

Training and education

• Annual NMD short courses
• Specialist NMD programs
• European NMD curriculum
• Training events
• Clinical evaluator training
• GCP and trial design training
• Call for expert trainers

Regulatory affairs database

Resources for researchers

• SOPs for mdx mouse and GRMD dog
• SOPs for SMA mice
• SOPs for CMD mice